News

Gene Therapy

Advances in production of retinal cells for treating blindness

AdvancesInProductionOfRetinalCellsForTreatingBlindness
Researchers discovered a way to refine the production of retinal cells from embryonic stem cells for treating blindness in the elderly. Using the CRISPR/Cas9 gene editing, they have also managed to modify the cells so that they can hide from the immune system to prevent rejection

Curing genetic disease in human stem cells

CuringGeneticDiseaseInHumanStemCells
The aim is to repair the error in the DNA without cutting it. This theoretically makes it a safer form of genetic editing. Scientists have shown for the first time that this technique can effectively and safely repair the DNA of stem cells derived from cystic fibrosis patients in the lab