So far, gene therapy has only treated rare disorders. Now, for the first time, it has been used to treat a boy with sickle cell disease, a common genetic disease
Delivering a functional gene to the ears of mice with a genetic hearing disorder allows them to detect sound
Some people have mutations that greatly lower their cholesterol. Tests in mice suggest gene editing could give the rest of us the same protection
New method could attack aggressive cancers like glioblastoma
Gene editing can already treat human diseases, but while editing the germline and enhancing human traits might be acceptable one day, we’re not there yet, says report
Scientists hope to “impart life with new forms and functions”
Gene-edited cells kill cancers
Immune cells engineered to target cancer could provide an off-the-shelf therapy